News Archive

ASGCT Conference

Three of our GTI leaders, Chamindra Laverty, Alysson Muotri, and Stephanie Cherqui, presented at the 27th Annual American Society for Gene and Cell Therapy in Baltimore Maryland this May. Topics covered lessons about clinical efficacy and safety of AAV gene therapy, brain organoid applications in gene therapy, and the bench- to- bedside- to- bench feedback loop that advances ex vivo gene therapy.

RARE Drug Development Symposium

GTI Director of Research Engagement, Betty Cabrera, was a panel member for a RARE Drug Development Symposium session in Philadelphia focused on emerging commercial and non-profit financing models of preclinical drug development. GTI highlighted how UCSD investigators are demonstrating that rare disease research can lead to applications to more common diseases. 

RARE Revolution Magazine - Spring edition, Issue 027

Rare Revolution: To bring about a dramatic and wide reaching change in conditions and attitudes for the rare disease community.

The Women in RARE edition highlights the women involved with working on rare diseases. Dr. Cherqui was interviewed about her journey in gene therapy, leading to the culmination of the Gene Therapy Initiative.

Read the article here.

UC San Diego Chancellor's Medal Awarded to Geoffrey and Nancy Stack

The University of California San Diego announced the recipients of the 2023 Chancellor's Medal and Lifetime Legacy Award. The recipients have all helped advanced health care and medicine in unique, impactful ways.

Nancy and Geoffrey Stack founded the Cystinosis Research Foundation in 2003. They also helped launch the UC San Diego Gene Therapy Initiative in 2023.

Read the article here.

San Diego Business Journal Women of the Year 2023 Finalists

San Diego Business Journal delivers the market’s most complete package of business news and information on San Diego County’s companies, industries and business people. SDNJ covers commercial real estate, banking and finance, biotech, health care, technology, defense, tourism, manufacturing, professional services and more.

Dr. Stephanie Cherqui was honored as a nominee for Woman of the Year 2023.

Read the article here.

UC San Diego Launches Gene Therapy Initiative

UC San Diego launches the Gene Therapy Initiative. The GTI is lead by codirectors Dr. Stephanie Cherqui and Dr. Alysson Muotri. The initiative will bring together key investigators, clinicians, knowledge and resources to foster new discoveries and chart the path forward for progress in gene therapy.

Read the article here.

UCSD launches Gene Therapy Initiative with help of $5 million gift from Stack foundation

A $5 million gift from Nancy and Geoffrey Stack will support the launch of UC San Diego's Gene Therapy Initiative. Nancy and Jeff have supported the research on cystinosis following their daughter's diagnosis. The Stacks hope that their gift will help further the future of gene therapy.

Read the article here.