2024
Impact Report
This report highlights the key milestones that have laid a strong foundation for the future of gene therapy at UC San Diego.
View ReportStephanie Cherqui and Natalie's Wish: Finding a Gene Therapy for Cystinosis
The story of what has driven UC San Diego's Stephanie Cherqui to develop a gene therapy for Cystinosis, a devastating inherited condition.
Our Impact in Advancing Gene Therapy
Through advanced, personalized gene therapies, we aim to alleviate and potentially cure a wide range of genetic disorders.
Empowering Innovation Through Seed Grants
Fueling early-stage research in gene therapy, giving pioneering scientists the resources they need to explore bold ideas and accelerate breakthroughs.
Connect, Learn, and Collaborate
From workshops and symposia to networking opportunities, our events bring together leaders in gene therapy to share knowledge, spark collaboration, and inspire the next wave of innovation.
Stay Informed with the Latest GTI Updates
Centralized archive of GTI articles, featuring updates on scientific discoveries, clinical progress, and program highlights in gene therapy research.